Drug boosts growth in youngsters with most common form of dwarfism

A new drug that helps regulate bone development has boosted growth rates in children with achondroplasia - the most common type of dwarfism – in a global trial led by MCRI.

Lead author and MCRI clinical geneticist Professor Ravi Savarirayan explains the results of the trial, which have been published in the New England Journal of Medicine.

dwarfism